The Platform Vector Gene Therapies (PaVe-GT) Project: Increasing the Efficiency of Adeno-Associated Virus (AAV) Gene Therapy Clinical Trial Startup

Upcoming Scheduled Maintenance

Please be advised that this application will be unavailable due to scheduled maintenance from June 18, 2026 at 5:00 PM ET through June 21, 2026. During this time, users will not be able to access the system. Please plan your work accordingly. We apologize for any inconvenience and appreciate your patience.

U.S. Department of Health and Human Services

National Institutes of Health

National Center for Advancing Translational Sciences

This article describes the challenges in developing gene therapies and the goal of the PaVe-GT program.

Human Gene Therapy | October 16, 2020